Now, here we go.
One-off injection may drastically reduce heart attack risk
Doctors hope to trial gene therapy on people with rare disorder in next three years
The old Crispr-Cas9. This finds and then disables PCSK9 or a similar gene. The aim is to turn off about 30% to 40% of PCSK9 to mimic the natural mutation that protects against heart attacks.
theguardian.com/science/201...
theguardian.com/science/201...
If the can turn off PCSK9, I hope they get a move on and turn on ABCD1 or 2 some time soon. Plenty of money in curing heart disease, but the knock-on effects have to trickle down to us.
Just a matter of sooner or later.