Experiences with

Gene therapy

🙂 UK TIME…..7.30PM Join NAF on August 22nd at 1:30 pm CDT for our webinar on Gene Therapy. In this session, Dr. Carolyn Yrigollen will teach us what gene therapy is, the different types of gene therapy, and how gene therapy could be used to treat Ataxia in the future.

https://parkinsonsnewstoday.com/news/aav-gad-gene-therapy-eases-parkinsons-symptoms-early-study/ "Treatment with the experimental gene therapy AAV-GAD led to significant easing of motor symptoms and improved life quality for most people with Parkinson’s disease in an early clinical trial, according to

https://parkinsonsnewstoday.com/news/anew-medical-advance-development-klotho-gene-therapy/?

https://www.apdaparkinson.org/article/gene-therapy-for-parkinsons-disease-3/

We start having the technology to deliver gene therapy...if we start also having a better idea about how our own cells works we get better and better https://scitechdaily.com/astonishing-scientists-unveil-first-blueprint-of-the-most-complex-molecular-machine-in-human-biology/

https://uk.finance.yahoo.com/news/first-gene-therapy-prevalent-pathologies-060000901.html

I know it's not PD but it is a neurological condition and sounds like a hopeful developmentUK toddler has hearing restored in world first gene therapy trial https://www.theguardian.com/science/article/2024/may/09/uk-toddler-has-hearing-restored-in-world-first-gene-therapy-trial?CMP=share_btn_url

Attendees will hear a first-hand account of the journey to receive a gene therapy from a person living with Parkinson’s disease.

Attendees will hear a first-hand account of the journey to receive a gene therapy from a person living with Parkinson’s disease.

The investigational gene therapy for the treatment of Parkinson’s disease was well tolerated with no serious adverse events that were considered related to AB-1005 in all 11 patients at 18 months.

Gene therapy specialist Meiragtx Holdings plc got a market bump courtesy of newly released top-line data from its phase II bridging study in Parkinson’s disease.

To demonstrate that the new platform could deliver the genetic payload without being intercepted by the liver, Lewis’ team created a gene therapy using a protein that aids in muscle development, often associated with a particularly muscular breed of cattle known as Belgian Blues.

The bilateral infusions of AB-1005 were well tolerated, without any SAEs linked to the gene therapy or contrast agent.

'eurologyLioe https://www.neurologylive.com/view/realistic-expectations-limitations-gene-therapy-parkinson-disease-ignacio-mata

I have mentioned to my doctor about things such as inner hair cell regeneration, gene therapy. Been told it’s not finalised will take 10 years. I was upset. I have seen many things online about people on trials and successful treatments for hearing loss. So when I mentioned I got turned away.

Anyone know how this study is going? I did a google search and there was something posted a few days ago but you had to buy the report. $500. I’m very interested but information seems hard to come by. It doesn’t sound like it would repair damage but stop or slow the disease. I wonder if it would eliminate

And people thought it was undruggable....they have already filed for a patent 😲 Researchers developed nanoparticles that can deliver a special type of gene therapy directly to cancer cells in the liver.

iPSCs and Dopaminergic Neuron Precursor Cells for Parkinson's Disease Presenter: Daniel Fremgen Director, Analytical Development, Aspen Neuroscience Time: 10:30 - 11:30am PT https://www.prnewswire.com/news-releases/aspen-neuroscience-to-present-at-international-society-for-cell--gene-therapy-isct-annual-meeting

Needless to say, once leriglitazone becomes FDA-approved, I manage to get in vivo gene therapy, or I end up with cerebral involvement and get HPSCT, I won't be taking pioglitazone anymore.

But now Tinkler has a chance of her condition going into remission — thanks to a groundbreaking gene therapy trial on the NHS. She is one of three patients to receive CAR T-cell therapy, which researchers hope can remove the need for lupus patients to take lifelong drugs.