Experiences with

Gene therapy

another PD trial by bayer https://www.bayer.com/media/en-us/first-participants-randomized-in-askbio-phase-ii-gene-therapy-trial-for-parkinsons-disease/

🙂 UK TIME…..7.30PM Join NAF on August 22nd at 1:30 pm CDT for our webinar on Gene Therapy. In this session, Dr. Carolyn Yrigollen will teach us what gene therapy is, the different types of gene therapy, and how gene therapy could be used to treat Ataxia in the future.

https://parkinsonsnewstoday.com/news/aav-gad-gene-therapy-eases-parkinsons-symptoms-early-study/ "Treatment with the experimental gene therapy AAV-GAD led to significant easing of motor symptoms and improved life quality for most people with Parkinson’s disease in an early clinical trial, according to

We start having the technology to deliver gene therapy...if we start also having a better idea about how our own cells works we get better and better https://scitechdaily.com/astonishing-scientists-unveil-first-blueprint-of-the-most-complex-molecular-machine-in-human-biology/

There are experimental treatments that help better control afib or even cure it, like gene therapy. But information is scarce. From what I understand, there isn't much interest from big pharma to create a pill that cures afib.

Gene therapy specialist Meiragtx Holdings plc got a market bump courtesy of newly released top-line data from its phase II bridging study in Parkinson’s disease.

Presenters will highlight advances in cell and gene therapies, including basic research discoveries and the latest clinical trials. Attendees will hear a first-hand account of the journey to receive a gene therapy from a person living with Parkinson’s disease.

https://parkinsonsnewstoday.com/news/anew-medical-advance-development-klotho-gene-therapy/?

https://www.apdaparkinson.org/article/gene-therapy-for-parkinsons-disease-3/

Presenters will highlight advances in cell and gene therapies, including basic research discoveries and the latest clinical trials. Attendees will hear a first-hand account of the journey to receive a gene therapy from a person living with Parkinson’s disease.

To demonstrate that the new platform could deliver the genetic payload without being intercepted by the liver, Lewis’ team created a gene therapy using a protein that aids in muscle development, often associated with a particularly muscular breed of cattle known as Belgian Blues.

https://uk.finance.yahoo.com/news/first-gene-therapy-prevalent-pathologies-060000901.html

The investigational gene therapy for the treatment of Parkinson’s disease was well tolerated with no serious adverse events that were considered related to AB-1005 in all 11 patients at 18 months.

I know it's not PD but it is a neurological condition and sounds like a hopeful developmentUK toddler has hearing restored in world first gene therapy trial https://www.theguardian.com/science/article/2024/may/09/uk-toddler-has-hearing-restored-in-world-first-gene-therapy-trial?CMP=share_btn_url

Needless to say, once leriglitazone becomes FDA-approved, I manage to get in vivo gene therapy, or I end up with cerebral involvement and get HPSCT, I won't be taking pioglitazone anymore.

But now Tinkler has a chance of her condition going into remission — thanks to a groundbreaking gene therapy trial on the NHS. She is one of three patients to receive CAR T-cell therapy, which researchers hope can remove the need for lupus patients to take lifelong drugs.

I have mentioned to my doctor about things such as inner hair cell regeneration, gene therapy. Been told it’s not finalised will take 10 years. I was upset. I have seen many things online about people on trials and successful treatments for hearing loss. So when I mentioned I got turned away.

The bilateral infusions of AB-1005 were well tolerated, without any SAEs linked to the gene therapy or contrast agent.

iPSCs and Dopaminergic Neuron Precursor Cells for Parkinson's Disease Presenter: Daniel Fremgen Director, Analytical Development, Aspen Neuroscience Time: 10:30 - 11:30am PT https://www.prnewswire.com/news-releases/aspen-neuroscience-to-present-at-international-society-for-cell--gene-therapy-isct-annual-meeting

The objective of this meeting is to understand what patients, and caregivers of patients in the pre-symptomatic or early stages of disease take into consideration when deciding whether to enroll in a gene therapy clinical trial and potentially receive an investigational gene therapy product.