A good friend of mine was diagnosed yesterday with AMN.
He already started having symptoms two years ago when he couldn't run more than a kilometer, and since then got a little worse. Today he can't run, and walks quite slowly with difficulties.
1) I have read in some researches that a successful Gene Therapy was conducted on two children with ALD and the levels of accumulated VLCFA were drastically reduced and the ALDP protein restored.
What's going on with that? seems pretty awesome. Do you think there is a chance in the near future that a gene therapy can treat this disease?
2) Also, I read that there is a process of remyelination, the can actually restore the damaged myelin and reverse the damage so that the person can actually walk normally.
Thank you all for the support and help.