More Gene Therapy Breakthroughs: Now, here we go... - AMN EASIER

AMN EASIER

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More Gene Therapy Breakthroughs

monkeybus profile image
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Now, here we go.

One-off injection may drastically reduce heart attack risk

Doctors hope to trial gene therapy on people with rare disorder in next three years

The old Crispr-Cas9. This finds and then disables PCSK9 or a similar gene. The aim is to turn off about 30% to 40% of PCSK9 to mimic the natural mutation that protects against heart attacks.

theguardian.com/science/201...

theguardian.com/science/201...

If the can turn off PCSK9, I hope they get a move on and turn on ABCD1 or 2 some time soon. Plenty of money in curing heart disease, but the knock-on effects have to trickle down to us.

Just a matter of sooner or later.

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monkeybus
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JasonHarnum profile image
JasonHarnum

always can count on you MonkeyBus for sharing out of the box ideas. Thx :)

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