Gene therapy

[WinnieThePoo]

I know it's not PD but it is a neurological condition and sounds like a hopeful developmentUK toddler has hearing restored in world first gene therapy trial theguardian.com/science/art...

[Boscoejean]

a lot of details in this article

bbc.com/news/health-68921561

[redhawk1]

Great news! My nephew has been deaf since birth. Hoping this monumental breakthrough will help him to be a part of the hearing world as well! And, such an important medical development that will usher in a whole new meaning of the word “cure”.

[pdpatient in reply to redhawk1]

redhawk1 I feel so sorry for your nephew. I hope and pray for you and your family and wish you all the best with this new advance in medicine.

As the proud uncle of my toddler nephew who I adore a lot I felt quite moved by your enthusiasm. May God bless you all.

[vwolff]

Very cool

[gomelgo]

am I missing something? Wondering how the procedure was done. Infusion? Surgery?

[Ghmac in reply to gomelgo]

me too

[WinnieThePoo]

DB-OTO is a gene therapy that has been created to deliver a working version of the OTOF gene to the inner ear. The DB-OTO injection is given into the inside of the ear during a surgical procedure that takes place under general anesthesia. This surgery is similar to cochlear implant surgery, which is well-established and has been used since the 1960s to treat deafness in babies.