Really exciting report of disease reversal in children with AADC (aromatic L-amino acid decarboxylase deficiency); article mentions same delivery technique is being used for GDNF gene therapy in Parkinson's.
Gene therapy for genetic disorder affecti... - Cure Parkinson's
Gene therapy for genetic disorder affecting brain dopamine metabolism shows success; same delivery technique being investigated for PD
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Rhyothemis
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Thanks for sharing. This is very encouraging.
“I’ve been investigating therapeutic gene therapy approaches for Parkinson’s disease for nearly 30 years, and this marks a significant milestone that may lead to major therapeutic opportunities,” says Dr. Bankiewicz, who founded the biotech startup Brain Neurotherapy Bio Inc. in 2018 to develop gene therapies for neurological disorders.
Bankiewicz and his team hope the Parkinson’s gene therapy surgery — a one-time treatment — provides ongoing benefits to slow disease progression.
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Gene therapy is underway!
https://parkinsonsnewstoday.com/2021/02/26/biogen-sangamo-partners-developing-novel-gene-therapies/
Replace or reorganize neurons
Can someone explain :Does the parkinson's glove therapy assume we don't have a loss of Dopa. Neurons
2021 Should be An Informative Year
it is hoped that gene therapy could offer a one-time cure for Parkinson’s.
https://www.evaluate.com
What improvements can we anticipate within 10-15 years?
DBS are being trialed at UCSF.
I hope for gene therapy but I think that is likely more like 20 +...