Gain Therapeutics

[tacato]

Any thoughts? Is there a reason that we should view this with any less skepticism as any other preclinical "breakthrough"? globenewswire.com/news-rele...

[park_bear]

This is for GBA1-associated Parkinson’s Disease. Approximately 5% of PD patients carry a GBA1 mutation.

exonpublications.com/index....

[Romulus13 in reply to park_bear]

Increasing GCase could also be applicable for idiopathic PD as well. This why Ambroxol study will recruit idiopathic PD patients.

That said this is a mouse model so nothing is certain yet.

[Boscoejean]

I was a bit disappointed that there was not more information on having any clinical trials outside Australia but I suppose it all depends on how that goes.