Forbes magazine: Though Promising, Gene T... - Cure Parkinson's

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Forbes magazine: Though Promising, Gene Therapies Face Durability And Reimbursement Headwinds

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The promise of gene therapy is to cure diseases associated with faulty or missing genes.

Ideally, gene therapies address the root causes of disease with a single curative dose. If they can replace a lifetime of expensive maintenance treatments this may lead to cost savings in the long run. Yet, the high upfront costs, uncertainty surrounding long-term durability, and adverse events have led to some concerns among payers and regulators.

Pharmaceutical firms deploy multiple approaches to pursuing curative gene therapy, including:

Replacing a mutated gene that causes disease with a healthy copy;

Inactivating a mutated gene;

Introducing a new gene into the body.

forbes.com/sites/joshuacohe...

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