Min-102

[Tim76]

Here’s some very exciting news:

pharmiweb.com/press-release...

[monkeybus]

Being it on.

[bluejadedwho]

Not to be negative, but it will then take another 5 years or more to become available in Canada....😔

[SongStream]

Very exciting! As one who is participating in the advance trial concluding the end of the year, I'm looking forward to receiving the actual drug. Another key note is "the only available alternative for cALD patients is hematopoietic stem cell transplantation (HSCT). This approach does not prevent the development of the AMN phenotype, for which there are no therapies available." This would be the only treatment available for AMN and Friedreich's Ataxia.

[KennyInPA in reply to SongStream]

Me too! The question of placebo still is on my mind and I'm looking forward to everyone getting the drug to see what happens.

[randal_mcdon]

Not much about results from the trial.

[DeanLM]

Thanks for posting this.