Experiences with

GM1 Gangliosidosis

gangliosidosis - Krabbe - MLD On Sunday, the Condition Management Day, we have presentations about Transitioning to Adult Services, Genetic Counselling, Long Term Impacts of Bone Marrow Transplant and much more...

Passage Bio are recruiting to two gene therapy trials: - Early onset and late onset infantile GM1 gangliosidosis Clinical trial information, including eligibility criteria: https://clinicaltrials.gov/ct2/show/NCT04713475 Register interest for participation in trial: https://www.pbgm01.com - Early