Dr. Scanlan from the Oregon Health & Science University is carrying out a study of sobetirome in X-ALD. He believes: “sobetirome may be beneficial to patients with ALD because it will stimulate the production of a gene product called ABCD2 which is very closely related to ABCD1, the defective gene in ALD patients, and ABCD2 can compensate for defective ABCD1. One measure of this compensation is reduction of the elevated VLCFA levels in ALD patients […] we also believe that sobetirome may arrest the progression of neurological symptoms in both cerebral ALD and AMN”. For more information about his research, please visit our research updates page: aldlife.org/news-research/r....
Your thoughts?
drugs for 8 years old boy suffering ALD
Genetic testing for under 16s
I have 3 sons who have just been diagnosed with ALD
I hate to ask but i need to know…how long after the disease sets in do male children have before they lose the battle with this disease?