I’m looking fro information on gene editing - Ataxia UK

Ataxia UK

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I’m looking fro information on gene editing

KENDALLENE profile image
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Gene editing

SCA

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KENDALLENE profile image
KENDALLENE
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sunvox profile image
sunvox

The closest to reality research is being done by Dr. Beverly Davidson at Children's Hospital of Philadelphia. If you email her directly she usually answers. At a minimum it's still a decade or more away. Ataxia's that are caused by an inherited gene mostly share a common trait of the production of a mutant protein. A far simpler treatment that is more likely coming soon will be to take a medication that cleans out the bad proteins.

chop.edu/news/gene-therapy-...

Stanleyclan profile image
Stanleyclan in reply to sunvox

Do you really think a protein cleaner (?😜!)will be available within a decade? I'm having a really negative week and feeling a bit hopeless😣🤔🙃

sunvox profile image
sunvox in reply to Stanleyclan

Yes, I most definitely do. People in very high places are finally getting a clue, and drugs for Huntington's are in clinical trial. Once they have success with those drugs I think the push to move to other similar disorders will be very quick.

Stanleyclan profile image
Stanleyclan in reply to sunvox

Thanks Joe....that lifts the spirits! Until then i will keep forcing the various suppliments down him 😁

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